Despite Problematic Phase 2 Data, CBER Director Says Muscular Dystrophy Gene Therapy Deserved Accelerated Approval

The FDA’s June 22 Accelerated Approval of Sarepta’s gene therapy Elevidys for Duchenne muscular dystrophy (DMD) is appropriate, despite an apparent disagreement within the department, according to CBER Director Peter Marks.
Source: Drug Industry Daily